Cure SMA is dedicated to the treatment and cure of spinal muscular atrophy (SMA)-a disease that takes away a person’s ability to walk, eat, or breathe. It is the number one genetic cause of death for infants.
Since 1984, we’ve directed and invested in comprehensive research that has shaped the scientific community’s understanding of SMA. We are currently on the verge of breakthroughs in treatment that will strengthen our children’s bodies, extend life, and lead to a cure.
We have deep expertise in every aspect of SMA-from the day-to-day realities to the nuances of care options-and until we have a cure, we’ll do everything we can to support children and families affected by the disease.
Learn more about how you can help us reach a treatment and cure at www.cureSMA.org.
Excuse me, what is the baseline anti-AAV9 antibody titers, if 1:50 could be effective to use the zolgensma, look forward your response, thank you a lot.
Pete is honest, up-front, smart and capable and he seems to genuinely care about all people. It's heartening to see a government official with competence, dignity and values. We are fortunate to have him.
really appreciate the work that will be done in this space. It is extremely important that we make travel more accessible and easy versus always a nightmare waiting to happen. Thank you
I am from Algeria. I have a daughter who suffers from spinal muscular atrophy. She is 7 months old. She is now suffering silently and is dying slowly... In countries where I am not even aware of the disease... knowing that I have a child who died in 2019 with the same disease.... Can you help me and sponsor With the treatment of my daughter, I lost all means, and I could no longer bear to see her get tired and die, as is the case with her brother.
I am from Algeria. I have a daughter who suffers from spinal muscular atrophy. She is 7 months old. She is now suffering silently and is dying slowly... In countries where I am not even aware of the disease... knowing that I have a child who died in 2019 with the same disease.... Can you help me and sponsor With the treatment of my daughter, I lost all means, and I could no longer bear to see her get tired and die, as is the case with her brother.
Also, parents who cannot afford much are usually on Medicaid - which would cover care. As long as the parents are proactive and take advantage of these things, it wouldn't be an issue. If not, they'd just get a huge bill in the mail every month.
This therapy was never mentioned when my niece was diagnosed with sma type 1 . She died at 7 months even with the therapy her bill exceeded 1 million dollars.
Giving thanks to #DRUROKO is something I will always take personal because he brought me back to my full health... ru-vid.com/show-UCWFpuQgd-AZ8UTmlwLOJiiw..
Giving thanks to #DRUROKO is something I will always take personal because he brought me back to my full health... ru-vid.com/show-UCWFpuQgd-AZ8UTmlwLOJiiw..
You’re so authentic and beautiful Dr Sunday,I recommend #DrOseghaleSundayHerbalHome medicine for y’all suffering from hsv1/2 or any other diseases, I’m a living witness thank you truly..🙏
You’re so authentic and beautiful Dr Sunday,I recommend #DrOseghaleSundayHerbalHome medicine for y’all to cure hsv1/2 or any other diseases, thank you truly..