Following many years of scientific research, it's expected that gene therapies may start to become a potential treatment option in the not-so-distant future. But the process of getting these new types of treatments to the right people could be challenging. We met with Pfizer and other health experts, to discuss the opportunities and challenges, and hear more about the ways in which our healthcare system could evolve to support sustainable access to these treatments for people living with rare diseases.
To watch the full programme, please visit raredisease.org.uk/careforrare
Rare Disease UK is the official organiser of Rare Disease Day in the UK. It is a campaign run by the charity Genetic Alliance UK, the largest alliance of organisations supporting everyone affected by genetic, rare and undiagnosed conditions in the UK.
#CareForRare #RareDiseases #RareDiseaseDay2023
27 фев 2023
