Taysha has released a video update about their gene replacement clinical trial for Rett syndrome - the REVEAL Adult Study. Taysha's Rett program, TSHA-102, is the first gene therapy clinical trial for Rett and got its start through RSRT's Gene Therapy Consortium and MECP2 Consortium.
The trial protocol is available here clinicaltrials....
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The Rett Syndrome Research Trust is singularly focused on a cure for Rett syndrome. Achieving success takes a deep understanding of the relevant science, an environment built for scientific collaboration, and experience with drug and business development. Today we are building on incredible scientific and industry momentum by implementing six genetic-based strategies that tackle Rett from every angle. Every single company pursuing a cure for Rett is able to do so because they leveraged discoveries and resources that were generated with RSRT funding. RSRT is the home of the Rett cure community, and we are confident that together we will cure Rett syndrome.
16 сен 2024
