Clinical Trials: Two Children Screened; One Qualifies, Antibodies Exclude the Other 

In this video, a mother of two children with Sanfilippo Syndrome discusses the screening process, explains that her younger child, a son, met the inclusion criteria but then screened positive for antibodies to the vector and was excluded. She discusses isolating her other child so as not to risk her exposure to the virus and developing the antibodies during her screening.