Development of Global Consensus Clinical Care Guidelines for Sanfilippo Syndrome, WORLDSymposium2023 

Dr. Cara O'Neill, Chief Science Officer of Cure Sanfilippo Foundation, speaking about how the first-ever global consensus clinical care guidelines for Sanfilippo syndrome were developed during a platform presentation at WORLDSymposium 2023.
To the audience of thousands, Dr. O'Neill shared why the guidelines are important, the study framework, the process of achieving consensus from experts around the world, what is included in the guidelines, and examples of the real-life impact the guidelines are already having on children with Sanfilippo.
Access the freely-available guidelines:
rdcu.be/cYqUj
Learn more about Sanfilippo syndrome:
curesanfilippo...