Learn about glucocorticoids - the standard of care for treatment of patients with Duchenne muscular dystrophy (DMD) - and their long-term impact on clinically meaningful disease progression milestones. This video covers the fundamentals of non-genetic and genetic-based therapies for patients with DMD, including small molecule therapies, cell-based therapy, exon skipping therapies, and gene transfer therapies.
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This education is designed for healthcare professionals involved in the management of patients with Duchenne Muscular Dystrophy including neurologists and other neuromuscular specialists and is supported by an independent medical educational grant from Sarepta Therapeutics.
22 апр 2024