Gene Therapy for Duchenne Muscular Dystrophy: Cash’s Story

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Children’s Hospital of Philadelphia now offers the first-ever gene therapy treatment for Duchenne Muscular Dystrophy (DMD) to patients like 6-year-old Cash. This breakthrough treatment slows the progression of symptoms and can improve strength and endurance for patients with DMD.

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30 окт 2023

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Комментарии : 40

@petersampson5202 9 месяцев назад

DEAR CASH & EVERYONE AT CHILDREN'S HOSPITAL OF PHILADELPHIA, GOD BLESS YOU MY FRIENDS. I AM VERY PROUD OF YOU AND VERY HAPPY FOR YOU. I HOPE ALL OF YOUR DREAMS COME TRUE. 🙏 I LOVE YOU SO VERY MUCH. 🙏 GOD BLESS YOU SO VERY MUCH CASH. 🙏 I LOVE CHILDREN'S HOSPITAL OF PHILADELPHIA SO VERY MUCH. 🙏 SINCERELY PETER

@elmehdiamine9103 5 месяцев назад

My son 6 years was the same hospital with the same doctor he hase dmd too I hope God help all the kids and parent too

@petersampson5202 5 месяцев назад

@@elmehdiamine9103 GOD BLESS YOUR SON. GOD BLESS ALL OF THE BEAUTIFUL DOCTORS. GOD BLESS ALL OF THE BEAUTIFUL PARENTS. GOD BLESS EVERYONE AT CHILDREN'S HOSPITAL OF PHILADELPHIA. I LOVE THE CHILDREN'S HOSPITAL OF PHILADELPHIA SO VERY MUCH. I WILL PRAY FOR EVERYONE. 🙏

@sarabnagra3456 2 месяца назад

How much does this cost?

@chukwudiobinna3079 8 месяцев назад

Great hope. Well done breakthrough makers

@natashaayudan5791 5 месяцев назад

I wish older children could get it I would give anything to stop my sons rate of progression I hate this disease so much

@HanifKhan-ui7ht 6 месяцев назад

Iam from Guyana my grandson is 10 years old he have dmd he is not walking we need help for him

@rajarani479 5 месяцев назад

my son is 9 years old he is DMD patient (7 exon is deletion) in genetic report im in pakistan please help me 😢

@rituchoudhary1699 2 месяца назад

Is there gene therapy for kcnq2 gene varients ??

@user-vx5np7qz7r 5 месяцев назад

My son is ten year old with DMD I am from Mauritius .He stop walking since last year please help if there is any treatment let me know.

@ChildrensHospPhila 5 месяцев назад

Hello. Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6052cRRYm for additional information.

@user-pu1si4mv4l 2 месяца назад

My brothers son ( 13 years old ) having this but we dont have treatment in Sri Lanka.we need help and guide from youll.

@ChildrensHospPhila 2 месяца назад

Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6052YXeXr for additional information.

@sarabnagra3456 2 месяца назад

My sister's son in DMD exons 48-52 deletion.He is 2 year's 11 months old. please hlp me what is suitable treatment for him. I am form Punjab

@ChildrensHospPhila 2 месяца назад

Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6051YbU41 for additional information.

@rituchoudhary1699 2 месяца назад

Did you get any treatment for your sister's son ? Plz tell if any

@yangweichen-rp9gx 4 месяца назад

I am from China. My son is DMD patient. He is 5 years old. Is it possible to cure? And how much would be the cost?❤

@ChildrensHospPhila 4 месяца назад

@yangweichen-rp9gx 4 месяца назад

@@ChildrensHospPhila Thanks for your feedback.I will check it out

@jaysimoes3705 5 месяцев назад

Yes great and all. I want to see results, of course I can find some results but I would like to see much more results and since what I have seen (have been shown?) are results within months we should be able to see these in more kids. Not just a few.

@LGRacing123 3 месяца назад

Im from Srilanka .My son also suffering from DMD.now he's 8years old.still he is working slowly .please please help me if there is any possibility .thank tou .

@ChildrensHospPhila 3 месяца назад

Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6050Y6icC for additional information.

@ramsita8198 7 месяцев назад

Wow good news

@Rashvanth2021 6 месяцев назад

My son 2years 11month old affect in DMD (14 exon is deletion or duplication) in gentic report. Please help me what is suitable treatment for my baby ( i am in India) please..... share me

@devikabai309 5 месяцев назад

Hi madam for Duchenne Muscular Dystrophy and every type of Dystrophy can give treatment in Nimhans Hospital in Bangalore

@ChildrensHospPhila 5 месяцев назад

Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6052iFuJk for additional information.

@jaysimoes3705 5 месяцев назад

Exon 14 can be tricky, so inform yourself. I think 1-9 and 17 so 14 should in theory be fine but again ask your specialist.

@Rashvanth2021 5 месяцев назад

14 exons (Exon 30 -43) deletion or duplication in genetic report

@bgmi_Moses 5 месяцев назад

I'm from India am DMD patient I'm 21years old help me to cure 😢

@ChildrensHospPhila 5 месяцев назад

Hi! Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6052cRRYm for additional information.

@balwantrajput4264 4 месяца назад

Hello . Can I get your contact no.

@ChildrensHospPhila 4 месяца назад

To explore treatment options at Children's Hospital of Philadelphia, please contact us at 1-800-879-2467 or visit our website ms.spr.ly/6054cmH3m.

@pickledbumblebeeviolinist 4 месяца назад

Our sons have Duchenne. They are 10 and 13. Any help or hope for them?

@ChildrensHospPhila 4 месяца назад

Thank you for contacting us. To explore treatment options at Children's Hospital of Philadelphia, please contact us at 1-800-879-2467 or visit our website ms.spr.ly/6056cQTaa.

@samaymeena5001 4 месяца назад

Please help my son is suffering ducchne muscular dystrophy since 8 years please help 😭😭 I am from India

@ChildrensHospPhila 4 месяца назад

@EdrianDometita-zb7wm 4 месяца назад

Hi I'm edrian from Philippines my brother suffere DMD since 7yr.old please help my brother

@ChildrensHospPhila 4 месяца назад

Please contact our Global Patient Services program to explore treatment options at Children’s Hospital of Philadelphia. You can call 1-267-426-6298 or visit ms.spr.ly/6050ctwEo for additional information.