Gene Therapy Today: What Pediatricians and Families Should Know 

Pediatric specialists from Columbia University Irving Medical Center, Weill Cornell Medicine, and NewYork-Presbyterian discuss the latest advances in gene therapy. This exciting new frontier offers the expansion of treatment options for a spectrum of diseases including blood disorders such as thalassemia, sickle cell anemia, hemophilia, and immune deficiency disorders. Our geneticists, hematologists, oncologists, and immunologists provide an update on the status of these new therapies relevant to practicing pediatricians, subspecialists, and healthcare providers. Panelists include Joshua Milner, MD, Director, Division of Allergy, Immunology, and Rheumatology, Professor of Pediatrics, Columbia; Sujit Sheth, MD, Chief, Division of Pediatric Hematology/Oncology, Vice Chair of Clinical Research, Professor of Clinical Pediatrics, Weill Cornell Medicine; Wendy Chung, MD, Chief, Division of Clinical Genetics, Medical Director, Columbia Genetic Counseling Graduate Program, Kennedy Family Professor, Columbia; Monica Bhatia, MD, Section Chief, Pediatric Stem Cell Transplant, Associate Professor of Pediatrics, Columbia; Catherine McGuinn, MD, Assistant Professor of Pediatrics, Weill Cornell Medicine.
This webinar is intended only to provide general information. Specific patient or clinical scenarios should be handled by patients’ practitioners based on their professional judgment, the needs of each patient and his/her unique circumstances, resources available where the patient is located, and other factors.