Day 1 - Part 2
“Moving Towards the Clinic” (Advancing Translational Programs) Session - Part 1 (0:25 - 57:35) | Ami Kamitani [International Project Unit at JCR Pharmaceuticals]; Haiyan Fu [Associate Professor, Gene Therapy Center, at University of North Carolina School of Medicine]; and Elizabeth Jalazo [Assistant Professor Genetics & Metabolism at University of North Carolina]; Srikanth Singamsetty [Scientific Director of Phoenix Nest]; joined by Mathias Schmidt [President and CEO of JCR USA] for Q&A
Resources and support available through Courageous Parents Network to help you find your way (1:00:35 - 1:25:52) | Jennifer Siedman [Director of Family Engagement at Courageous Parents Network | Parent of Child with Sanfilippo Type B]
Updates on Active Clinical Trials (Part 1) (1:30:10 - 2:35:40) | Mercé Pineda [Senior Neuropaediatrics Consultant at SJD Barcelona Children’s Hospital]; Thomas Mathers [Founder, President and CEO of Allievex Corporation]; and Emil Kakkis [Founder, President and Chief Executive Officer of Ultragenyx]
24 окт 2022
